Story
Thanks for visiting our JustGiving page, where your donation will support a pipeline of clinical trials of gene therapies for inherited sight loss.
Inherited sight loss affects around 1-in-3000 people and there are no treatments currently available. We are developing experimental therapies in which we deliver working copies of genes to cells in the eye using an engineered virus. We have shown proof-of-concept in the laboratory for many forms of inherited sight loss, and our first clinical trial showed that this technique is safe and can restore vision in a specific condition, Leber congenital amaurosis caused by damage to the RPE65 gene. More details of our work can be found on our website.
Translating proof-of-concept into clinical therapies for other forms of inherited sight loss requires significant investment, and we are seeking substantial support from charities and research councils. But we also need your support. Your generous donation – however big or small – will help us reach our goal of bringing a pipeline of gene therapies for sight loss to clinical trial. Currently we are seeking funding for an advanced purification system that we use to produce engineered virus for our laboratory experiments. Your donation can help us invest £10,000 in this essential equipment.
Just £5 would allow us to detect how well our experimental treatments are working in the lab, using DNA primers in a test called PCR. Any support is warmly welcomed.
Any amount of money will go a long way towards fulfilling these aims – we appreciate all of your donations! Should you wish to discuss your donation, or set up regular monthly payments to support our work, please email eye.info@ucl.ac.uk or call 0207 608 7982
Donating through JustGiving is simple, fast and totally secure. Your details are safe with JustGiving – they’ll never sell them on or send unwanted emails. Once you donate, they’ll send your money directly to us and make sure Gift Aid is reclaimed on every eligible donation by a UK taxpayer.
So please dig deep and donate now - we need your support to develop safe and effective cell therapies for sight loss caused by AMD and diabetic eye disease.